Department of Pediatrics > Genetics and Metabolism > Gene Therapy Program > Gene Therapy Program Faculty & Staff
Gene Therapy Program Faculty & Staff
Cores
Core A: Administrative Core
Chester B. Whitley,
Ph.D., M.D., Core Leader
- Laura Wolff, Senior Secretary
- David M. Brown, M.D., Consultant
- Carol J. Lusty, Ph.D., External Advisory Committee Consultant (Project I)
- Nicholas Muzyczka, Ph.D., External Advisory Committee Consultant (Project II)
- R. Michael Blaese, M.D., External Advisory Committee Consultant (Project III)
- Mark Kay, Ph.D., M.D., External Advisory
Committee Consultant (Project IV)
- Inder Verma, Ph.D., External Advisory Committee Consultant (Project V)
- Steven U. Walkley, D.V.M., Ph.D., External Advisory Committee Consultant (Project
V and Research Animal Care and Medicine Core)
Core B: Microchemical Facility
Eric Eccleston, Ph.D., Core Leader
Core C: Research Animal Care and Medicine Core
Cynthia Gillett, D.V.M., Core Leader
- Ronald Gunther, D.V.M., Research
Associate
- Brenda Koniar, Veterinary Technician
- Steven U. Walkley, D.V.M., Ph.D., Neuropathology Consultant
Core D: Cell Processing
Jeffrey McCullough, M.D., Core Leader
Core E: Real-time Quantitative PCR Facility
Dao Pan, Ph.D., Core Leader
Core F: Viral Vector Core
R. Scott McIvor, Ph.D., Core Leader
Projects
Project I: Therapy for Hyperammonemia with Genetically-Engineered Bacteria
Mendel Tuchman, M.D., Principal
Investigator
- Michael H. Malamy, Ph.D., Co-Investigator
- Hiroki Morizono, Ph.D., Research Work
- Carol J. Lusty, Ph.D., Consultant
Project II: Gene Therapy for Ataxia
R. Scott McIvor, Ph.D., Principal Investigator
- Walter C. Low, Ph.D., Co-Investigator
- Harry T. Orr, Ph.D., Co-Investigator
Project III: Chimeraplasty for Mutations Associated with Mental Retardation
Betsy T. Kren, Ph.D., Principal
Investigator
- Clifford Steer, M.D., Co-Investigator
Project IV: Sleeping Beauty Transposon for Gene Therapy
Perry Hackett, Ph.D., Principal
Investigator
Project V: Ex Vivo Lentiviral Hematopoetic Stem Cell Gene Therapy for MPS Type
I
Chester B. Whitley,
Ph.D., M.D., Principal Investigator
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